About-cancer/treatment/drugs/leukemia

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Drugs Approved for Leukemia

This page lists cancer drugs approved by the Food and Drug Administration (FDA) for leukemia. The list includes generic and brand names. This page also lists common drug combinations used in leukemia. The individual drugs in the combinations are FDA-approved. However, drug combinations themselves usually are not approved, but are widely used.

The drug names link to NCI's Cancer Drug Information summaries. There may be drugs used in leukemia that are not listed here.

Drugs Approved for Acute Lymphoblastic Leukemia (ALL)

Arranon (Nelarabine)

Asparaginase Erwinia chrysanthemi

Asparlas (Calaspargase Pegol-mknl)

Besponsa (Inotuzumab Ozogamicin)

Blinatumomab

Blincyto (Blinatumomab)

Calaspargase Pegol-mknl

Cerubidine (Daunorubicin Hydrochloride)

Clofarabine

Clolar (Clofarabine)

Cyclophosphamide

Cytarabine

Dasatinib

Daunorubicin Hydrochloride

Dexamethasone

Doxorubicin Hydrochloride

Erwinaze (Asparaginase Erwinia Chrysanthemi)

Gleevec (Imatinib Mesylate)

Iclusig (Ponatinib Hydrochloride)

Inotuzumab Ozogamicin

Imatinib Mesylate

Kymriah (Tisagenlecleucel)

Marqibo (Vincristine Sulfate Liposome)

Mercaptopurine

Methotrexate

Nelarabine

Oncaspar (Pegaspargase)

Pegaspargase

Ponatinib Hydrochloride

Prednisone

Purinethol (Mercaptopurine)

Purixan (Mercaptopurine)

Rubidomycin (Daunorubicin Hydrochloride)

Sprycel (Dasatinib)

Tisagenlecleucel

Trexall (Methotrexate)

Vincristine Sulfate

Vincristine Sulfate Liposome

Drug Combinations Used in Acute Lymphoblastic Leukemia (ALL)

Hyper-CVAD

Drugs Approved for Acute Myeloid Leukemia (AML)

Arsenic Trioxide

Cerubidine (Daunorubicin Hydrochloride)

Cyclophosphamide

Cytarabine

Daunorubicin Hydrochloride

Daunorubicin Hydrochloride and Cytarabine Liposome

Daurismo (Glasdegib Maleate)

Dexamethasone

Doxorubicin Hydrochloride

Enasidenib Mesylate

Gemtuzumab Ozogamicin

Gilteritinib Fumarate

Glasdegib Maleate

Idamycin PFS (Idarubicin Hydrochloride)

Idarubicin Hydrochloride

Idhifa (Enasidenib Mesylate)

Ivosidenib

Midostaurin

Mitoxantrone Hydrochloride

Mylotarg (Gemtuzumab Ozogamicin)

Rubidomycin (Daunorubicin Hydrochloride)

Rydapt (Midostaurin)

Tabloid (Thioguanine)

Thioguanine

Tibsovo (Ivosidenib)

Trisenox (Arsenic Trioxide)

Venclexta (Venetoclax)

Venetoclax

Vincristine Sulfate

Vyxeos (Daunorubicin Hydrochloride and Cytarabine Liposome)

Xospata (Gilteritinib Fumarate)

Drug Combinations Used in Acute Myeloid Leukemia (AML)

ADE

Drugs Approved for Blastic Plasmacytoid Dendritic Cell Neoplasm (BPDCN)

  • Elzonris (Tagraxofusp-erzs)
  • Tagraxofusp-erzs

Drugs Approved for Chronic Lymphocytic Leukemia (CLL)

Alemtuzumab

Arzerra (Ofatumumab)

Bendamustine Hydrochloride

Bendeka (Bendamustine Hydrochloride)

Campath (Alemtuzumab)

Chlorambucil

Copiktra (Duvelisib)

Cyclophosphamide

Dexamethasone

Duvelisib

Fludarabine Phosphate

Gazyva (Obinutuzumab)

Ibrutinib

Idelalisib

Imbruvica (Ibrutinib)

Leukeran (Chlorambucil)

Mechlorethamine Hydrochloride

Mustargen (Mechlorethamine Hydrochloride)

Obinutuzumab

Ofatumumab

Prednisone

Rituxan (Rituximab)

Rituxan Hycela (Rituximab and Hyaluronidase Human)

Rituximab

Rituximab and Hyaluronidase Human

Treanda (Bendamustine Hydrochloride)

Venclexta (Venetoclax)

Venetoclax

Zydelig (Idelalisib)

Drug Combinations Used in Chronic Lymphocytic Leukemia (CLL)

CHLORAMBUCIL-PREDNISONE

CVP

Drugs Approved for Chronic Myelogenous Leukemia (CML)

Bosulif (Bosutinib)

Bosutinib

Busulfan

Busulfex (Busulfan)

Cyclophosphamide

Cytarabine

Dasatinib

Dexamethasone

Gleevec (Imatinib Mesylate)

Hydrea (Hydroxyurea)

Hydroxyurea

Iclusig (Ponatinib Hydrochloride)

Imatinib Mesylate

Mechlorethamine Hydrochloride

Mustargen (Mechlorethamine Hydrochloride)

Myleran (Busulfan)

Nilotinib

Omacetaxine Mepesuccinate

Ponatinib Hydrochloride

Sprycel (Dasatinib)

Synribo (Omacetaxine Mepesuccinate)

Tasigna (Nilotinib)

Drugs Approved for Hairy Cell Leukemia

Cladribine

Intron A (Recombinant Interferon Alfa-2b)

Lumoxiti (Moxetumomab Pasudotox-tdfk)

Moxetumomab Pasudotox-tdfk

Recombinant Interferon Alfa-2b

Drugs Approved for Mast Cell Leukemia

Midostaurin

Rydapt (Midostaurin)

Drugs Approved for Meningeal Leukemia

Cytarabine